{"id":378,"date":"2014-03-27T17:41:38","date_gmt":"2014-03-27T16:41:38","guid":{"rendered":"http:\/\/s519078666.onlinehome.fr\/?page_id=378"},"modified":"2015-02-19T11:34:47","modified_gmt":"2015-02-19T10:34:47","slug":"essais-cliniques-sur-la-maladie-de-stargardt","status":"publish","type":"page","link":"http:\/\/www.stargardt.fr\/test\/recherche-et-etudes-en-cours\/essais-cliniques-sur-la-maladie-de-stargardt\/","title":{"rendered":"Essais cliniques sur la maladie de Stargardt"},"content":{"rendered":"<h2>Des essais cliniques encore rares<\/h2>\n<p><strong>Les essais cliniques sur la maladie de Stargardt sont peu nombreux.<\/strong>\u00a0Ils portent sur diff\u00e9rentes technologies : th\u00e9rapie g\u00e9nique, th\u00e9rapie cellulaire, pharmacologie. Certains sont en cours de r\u00e9alisation.<\/p>\n<p>Ces essais constituent de nouvelles \u00e9tapes dans la recherche d\u2019un traitement mais ne confirment pas aujourd\u2019hui l\u2019existence d\u2019un traitement sp\u00e9cifique efficace.<\/p>\n<p>On entend ici par essai clinique, une \u00e9tude m\u00e9dicale qui a pour objectif de v\u00e9rifier l\u2019efficacit\u00e9 et la tol\u00e9rance d\u2019un traitement chez l\u2019\u00eatre humain. Ces \u00e9tudes sont r\u00e9alis\u00e9es tout d\u2019abord en laboratoire en recherche fondamentale, puis sont test\u00e9s soit sur des mod\u00e8les cellulaires soit chez l\u2019animale en vue de faire des premiers tests de tol\u00e9rance (\u00e9tude de doses, d\u2019innocuit\u00e9, d\u2019efficacit\u00e9).<\/p>\n<p>Ensuite , les essais cliniques peuvent \u00eatre r\u00e9alis\u00e9s chez l\u2019Homme.<\/p>\n<p>Chaque essai clinique est con\u00e7u et r\u00e9alis\u00e9 en conformit\u00e9 aux r\u00e8gles \u00e9thiques \u00e9tablies par les institutions de sant\u00e9. Chaque personne incluse dans un essai clinique re\u00e7oit un suivi m\u00e9dicale et biologique tout au long de l\u2019essai selon un protocole pr\u00e9cis.<\/p>\n<p>&nbsp;<\/p>\n<p>Voici certains essais cliniques en cours dans la maladie de Stargardt (relev\u00e9 d\u00e9cembre 2014-Clinical trials))<\/p>\n<h4><span style=\"color: #003366;\">Th\u00e9rapie g\u00e9nique<\/span><\/h4>\n<p><a href=\"https:\/\/clinicaltrials.gov\/ct2\/show\/NCT01367444?term=stargardt&amp;rank=3\">Phase I\/IIa Study of StarGen in Patients With Stargardt Macular Degeneration<\/a>\u00a0(Phase I\/II* &#8211; Sponsor : Sanofi \u2013 Assay in USA and\u00a0France)<\/p>\n<h3><\/h3>\n<h4><span style=\"color: #003366;\">Th\u00e9rapie cellulaire<\/span><\/h4>\n<p><a href=\"http:\/\/clinicaltrials.gov\/ct2\/show\/NCT01345006?term=stargardt&amp;rank=5\">Sub-retinal Transplantation of hESC Derived RPE(MA09-hRPE)Cells in Patients With Stargardt&rsquo;s Macular Dystrophy<\/a> (Phase I\/II* ; Sponsor :Advanced Cell Technology \u2013 Assay in USA)<\/p>\n<p><a href=\"http:\/\/clinicaltrials.gov\/ct2\/show\/NCT01469832?term=stargardt&amp;rank=9\">Safety and Tolerability of Sub-retinal Transplantation of Human Embryonic Stem Cell Derived Retinal Pigmented Epithelial (hESC-RPE) Cells in Patients With Stargardt&rsquo;s Macular Dystrophy (SMD)<\/a> (Phase I\/II* &#8211; Sponsor : Advanced Cell Technology \u2013 Assay in UK)<\/p>\n<h3><\/h3>\n<h4><span style=\"color: #003366;\">Pharmacologie<\/span><\/h4>\n<p><a href=\"https:\/\/clinicaltrials.gov\/ct2\/show\/NCT01278277?term=stargardt&amp;rank=10\">Saffron Supplementation in Stargardt&rsquo;s Disease<\/a> (Pase I\/II* \u2013 Sponsor\u00a0: Catholic University of the Sacred Heart &#8211; Assay in Italy)<\/p>\n<p><a href=\"https:\/\/clinicaltrials.gov\/ct2\/show\/NCT00420602?term=stargardt&amp;rank=11\">DHA Supplementation in Patients With STGD3<\/a> (Phase I\/II* ; Sponsor: University of Utah. Assay in USA)<\/p>\n<h3><\/h3>\n<h4><span style=\"color: #003366;\">Autres techniques<\/span><\/h4>\n<p><a href=\"https:\/\/clinicaltrials.gov\/ct2\/show\/NCT01790958?term=stargardt&amp;rank=14\">Microcurrent Stimulation to Treat Macular Degeneration<\/a> <strong>( <\/strong>Sonsor\u00a0: Retina Institute of Hawaii \u2013 Assay in USA)<\/p>\n<p>&nbsp;<\/p>\n<p>*Phase I\/II = Safety\/Efficacy\u00a0Study<\/p>\n<p>&nbsp;<\/p>\n<p>Pour obtenir plus de d\u00e9tails sur \u00a0les \u00e9tudes en cours, nous vous conseillons de consulter les sites suivants :<\/p>\n<p><strong>Clinical trials<\/strong> regroupe de nombreux essais cliniques internationaux en cours<\/p>\n<p><a title=\"clinicaltrails.org\" href=\"https:\/\/clinicaltrials.gov\/ct2\/results?term=stargardt&amp;Search=Search\" target=\"_blank\">https:\/\/clinicaltrials.gov<\/a><\/p>\n<p><strong>Pubmed<\/strong> regroupe de nombreux articles scientifiques sur la recherche (fondamentale, exp\u00e9rimentale, clinique)<\/p>\n<p><a href=\"http:\/\/www.ncbi.nlm.nih.gov\/pubmed\" target=\"_blank\">www.ncbi.nlm.nih.gov\/pubmed<\/a><\/p>\n<div style=\"padding-bottom:20px; padding-top:10px;\" class=\"hupso-share-buttons\"><!-- Hupso Share Buttons - https:\/\/www.hupso.com\/share\/ --><a class=\"hupso_toolbar\" href=\"https:\/\/www.hupso.com\/share\/\"><img src=\"http:\/\/static.hupso.com\/share\/buttons\/lang\/fr\/share.png\" rel=\"PrettyPhoto[378]\" style=\"border:0px; padding-top: 5px; float:left;\" alt=\"Share Button\"\/><\/a><script type=\"text\/javascript\">var hupso_services_t=new Array(\"Twitter\",\"Facebook\",\"Google Plus\");var hupso_background_t=\"#EAF4FF\";var hupso_border_t=\"#66CCFF\";var hupso_toolbar_size_t=\"big\";var hupso_image_folder_url = \"\";var hupso_url_t=\"\";var hupso_title_t=\"Essais%20cliniques%20sur%20la%20maladie%20de%20Stargardt\";<\/script><script type=\"text\/javascript\" src=\"http:\/\/static.hupso.com\/share\/js\/share_toolbar.js\"><\/script><!-- Hupso Share Buttons --><\/div>","protected":false},"excerpt":{"rendered":"<p>Des essais cliniques encore rares Les essais cliniques sur la maladie de Stargardt sont peu nombreux.\u00a0Ils portent sur diff\u00e9rentes technologies : th\u00e9rapie g\u00e9nique, th\u00e9rapie cellulaire, pharmacologie. Certains sont en cours de r\u00e9alisation. Ces essais constituent de nouvelles \u00e9tapes dans la recherche d\u2019un traitement mais ne confirment pas aujourd\u2019hui l\u2019existence d\u2019un traitement sp\u00e9cifique efficace. On entend&#8230;<\/p>\n<div style=\"padding-bottom:20px; padding-top:10px;\" class=\"hupso-share-buttons\"><!-- Hupso Share Buttons - https:\/\/www.hupso.com\/share\/ --><a class=\"hupso_toolbar\" href=\"https:\/\/www.hupso.com\/share\/\"><img src=\"http:\/\/static.hupso.com\/share\/buttons\/lang\/fr\/share.png\" style=\"border:0px; padding-top: 5px; float:left;\" alt=\"Share Button\"\/><\/a><script type=\"text\/javascript\">var hupso_services_t=new Array(\"Twitter\",\"Facebook\",\"Google Plus\");var hupso_background_t=\"#EAF4FF\";var hupso_border_t=\"#66CCFF\";var hupso_toolbar_size_t=\"big\";var hupso_image_folder_url = \"\";var hupso_url_t=\"\";var hupso_title_t=\"Essais%20cliniques%20sur%20la%20maladie%20de%20Stargardt\";<\/script><script type=\"text\/javascript\" src=\"http:\/\/static.hupso.com\/share\/js\/share_toolbar.js\"><\/script><!-- Hupso Share Buttons --><\/div>","protected":false},"author":2,"featured_media":0,"parent":305,"menu_order":0,"comment_status":"closed","ping_status":"closed","template":"","meta":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v19.4 - https:\/\/yoast.com\/wordpress\/plugins\/seo\/ -->\n<title>Essais cliniques sur la maladie de Stargardt - Nouveau site test<\/title>\n<meta name=\"description\" content=\"Les essais cliniques sur la maladie de Stargardt sont peu nombreux. 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