1.0Stargardt Foundationhttps://www.stargardt.fr/enNathaliehttps://www.stargardt.fr/en/blog/author/nathalie/rich600338<blockquote class="wp-embedded-content"><a href="https://www.stargardt.fr/en/current-research-and-trials/orphan-drug/">“Orphan Drug” designation</a></blockquote> <script type='text/javascript'> <!--//--><![CDATA[//><!-- /*! This file is auto-generated */ !function(d,l){"use strict";var e=!1,n=!1;if(l.querySelector)if(d.addEventListener)e=!0;if(d.wp=d.wp||{},!d.wp.receiveEmbedMessage)if(d.wp.receiveEmbedMessage=function(e){var t=e.data;if(t)if(t.secret||t.message||t.value)if(!/[^a-zA-Z0-9]/.test(t.secret)){for(var r,i,a,s=l.querySelectorAll('iframe[data-secret="'+t.secret+'"]'),n=l.querySelectorAll('blockquote[data-secret="'+t.secret+'"]'),o=new RegExp("^https?:$","i"),c=0;c<n.length;c++)n[c].style.display="none";for(c=0;c<s.length;c++)if(r=s[c],e.source===r.contentWindow){if(r.removeAttribute("style"),"height"===t.message){if(1e3<(a=parseInt(t.value,10)))a=1e3;else if(~~a<200)a=200;r.height=a}if("link"===t.message)if(i=l.createElement("a"),a=l.createElement("a"),i.href=r.getAttribute("src"),a.href=t.value,o.test(a.protocol))if(a.host===i.host)if(l.activeElement===r)d.top.location.href=t.value}}},e)d.addEventListener("message",d.wp.receiveEmbedMessage,!1),l.addEventListener("DOMContentLoaded",t,!1),d.addEventListener("load",t,!1);function t(){if(!n){n=!0;for(var e,t,r=-1!==navigator.appVersion.indexOf("MSIE 10"),i=!!navigator.userAgent.match(/Trident.*rv:11\./),a=l.querySelectorAll("iframe.wp-embedded-content"),s=0;s<a.length;s++){if(!(e=a[s]).getAttribute("data-secret"))t=Math.random().toString(36).substr(2,10),e.src+="#?secret="+t,e.setAttribute("data-secret",t);if(r||i)(t=e.cloneNode(!0)).removeAttribute("security"),e.parentNode.replaceChild(t,e)}}}}(window,document); //--><!]]> </script><iframe sandbox="allow-scripts" security="restricted" src="https://www.stargardt.fr/en/current-research-and-trials/orphan-drug/embed/" width="600" height="338" title="““Orphan Drug” designation” — Stargardt Foundation" frameborder="0" marginwidth="0" marginheight="0" scrolling="no" class="wp-embedded-content"></iframe>“Orphan Drug”: a designation to ease research Several products in development for the treatment of Stargardt disease have received the “Orphan Drug” designation from the European Medicines Agency (EMA) or from the Food and Drug Administration (FDA, American Healthy Agency). These are products being studied (treatment trials) which have potential efficacy against the rare disease...